Pediatric Blood & Immune Disorders Clinical Trials

Clinical trials have formed the foundation of virtually every advance made in medical care. For some pediatric blood and immune disorders, clinical trials may offer hope where no hope existed before. MSK Kids is conducting clinical trials assessing new approaches for children with noncancerous blood and immune disorders, with a particular interest in gene therapy and improving stem cell transplantation for these young people.

Your child’s care team will let you know if your child is eligible to participate in a clinical trial. The decision to enroll is entirely voluntary. The study team will explain the benefits and risks of the study to you so you can make an informed decision.

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2 Clinical Trials found
A Study of Cord Blood Transplantation in Children and Young Adults with Blood Cancers and Non-Cancerous Blood Disorders
The transplantation of stem cells from umbilical cord blood is a treatment for some blood cancers and non-cancerous blood or metabolic disorders. Patients routinely receive high doses of chemotherapy and sometimes radiation before receiving the stem cells to help make room in the bone marrow for new blood stem cells to grow, prevent the body from rejecting the transplanted cells, and help kill any abnormal blood cells in the body. However, the combination of these treatments can have serious side effects.
New York City
A Study Using Immune Suppression Prior to Stem Cell Transplant for Children and Adults with Sickle Cell Disease or Beta-Thalassemia
Sickle cell disease and beta-thalassemia are blood diseases caused by a genetic change (mutation) in hemoglobin, the protein in red blood cells that carries oxygen throughout the body. People with these diseases may be offered a stem cell transplant. Stem cell transplantation involves receiving healthy blood-forming cells (stem cells) from a donor to replace the diseased or damaged cells in the bone marrow.
New York City, Commack, Basking Ridge, Westchester, Monmouth, Bergen, Nassau