Clinical trials have formed the foundation of virtually every advance made in medical care. For some pediatric blood disorders, clinical trials may offer hope where no hope existed before. MSK Kids is conducting clinical trials assessing new approaches for children with noncancerous blood disorders, with a particular interest in gene therapy and improving stem cell transplantation for these young people.
Your child’s care team will let you know if your child is eligible to participate in a clinical trial. The decision to enroll is entirely voluntary. The study team will explain the benefits and risks of the study to you so you can make an informed decision.